Gene therapy clinical trial yields promising results for Batten disease

Promising results from a team of NewYork-Presbyterian Hospital/Weill Cornell Medical Center physician-scientists show that gene therapy is both safe and effective at slowing the progression of Batten disease, or Late Infantile Neuronal Ceroid Lipofuscinosis (LINCL), a rare, genetic, degenerative neurological disorder that usually becomes fatal in children by the age of 8 to 12.

Get the full story...

Reply

The content of this field is kept private and will not be shown publicly.
  • Lines and paragraphs break automatically.
  • Allowed HTML tags: <p> <br> <a> <em> <ul> <ol> <li> <strong> <blockquote>

More information about formatting options

1 + 16 =
Solve this simple math problem and enter the result. E.g. for 1+3, enter 4.