Gene therapy slows progression of neurodegenerative disease in children

Gene therapy to replace the faulty CLN2 gene, which causes a neurodegenerative disease that is fatal by age 8-12 years, was able to slow significantly the rate of neurologic decline in treated children, according to a paper published online ahead of print in the May 2008 issue (Vol. 19 No. 5) of Human Gene Therapy, a peer-reviewed journal published by Mary Ann Liebert, Inc.

Get the full story...

Reply

The content of this field is kept private and will not be shown publicly.
  • Lines and paragraphs break automatically.
  • Allowed HTML tags: <p> <br> <a> <em> <ul> <ol> <li> <strong> <blockquote>

More information about formatting options

1 + 2 =
Solve this simple math problem and enter the result. E.g. for 1+3, enter 4.